Dr. Sharon Hesterlee reports back on MDF's involvement with the Muscular Dystrophy Coordinating Committee.
As a clinician and researcher, Dr. Benedikt Schoser of Ludwig-Maximilians University of Munich, Germany, is focused on how research findings can be translated into improved patient care - and how patient concerns can help guide researchers to new areas of interest.
For the second year in a row, MDF represented the DM community in Rare Disease Week activities on Capitol Hill and at the National Institutes of Health as part of the Rare Disease Legislative Advocates conference.
FDA's Orphan Drug Program is designed to encourage pharmaceutical companies to develop drugs for rare or 'orphan' diseases that might otherwise not be appealing to industry.
February is American Heart Month, and MDF has partnered with Drs. Katharine Hagerman and Marianne Goodwin to highlight important research on cardiac issues in myotonic dystrophy for our readers