Although fatigue represents a substantial burden in DM1, tools must be validated to assess its diverse contributing factors in order to develop clinical trial endpoints and effective therapies.
News
07/06/2017 - 3:11pm
Preclinical animal efficacy data used to support the scientific rational for Ionis’ phase 1/2 clinical trial in DM1 was just published.
07/06/2017 - 3:02pm
New fly models show a DM2 phenotype at least as severe as DM1 and may provide a platform for studies of genetic modifiers and candidate therapy screening in DM.
07/06/2017 - 2:53pm
A large retrospective study helps clarify genotype-cardiac phenotype relationships in adult DM1.
06/02/2017 - 4:29pm
A recent review article makes the case that DM is a brain disease and that better understanding of and treatment strategies for the neurological consequences of DM are essential.
