A novel genome editing strategy removes expanded CUG repeats in DMPK transcripts.
News
12/11/2018 - 8:30am
TREAT-NMD’s TACT process provides unbiased feedback on drug development programs in neuromuscular diseases.
11/06/2018 - 8:42am
DTI detects specific changes in the corticospinal tract, reflecting cortical gray matter volume reductions linked to DM1 motor function deficits.
11/06/2018 - 7:35am
Development, validation, and use of CNS clinical outcome assessments in DM1 must consider their interactions with other parameters of patient functioning.
11/06/2018 - 6:17am
An innate immune response pathway, the induction of interferon type 1, rather than activation of autophagy, is responsible for impaired myogenesis in CDM.
