Home / Community / News


10/03/2015 - 5:53pm

Many of you know that the Phase I/II clinical trial for a potential therapy, ISIS-DMPKRx, for people with myotonic dystrophy type 1 (DM1) has been underway since last December. The trial is still actively recruiting participants.

10/10/2015 - 6:44pm

The Clinical Trials Transformation Initiative (CTTI), a public-private partnership between Duke University and the FDA focused on increasing the efficiency of clinical trials, has released a detailed series of recommended best practices for interactions between patient groups and clinical trial sponsors.

10/10/2015 - 7:30am

MDF hosted the Myotonic Dystrophy Patient-Centered Therapy Development Meeting in Washington, D.C. on September 17, 2015. The regulatory workshop featured speakers from academia, industry and the FDA. 

10/03/2015 - 6:13pm

On September 18th, DM community leaders and their families from across the country visited with their Senators and Representatives urging action on the 21st Century Cures Act.  MDF is following up on this successful advocacy campaign with our first ever DM Congressional Call-In on October 13th.

09/23/2015 - 3:14pm

Every year, the MDF Conference provides a friendly, welcoming place for people with DM to learn from one another and hear from an incredibly diverse array of scientists, researchers, advocates and community members with one thing in common: a belief that every person with DM deserves a high quality of life, and that learning from each other strengthens us all.


© Myotonic Dystrophy Foundation. All rights reserved.