08/26/2015 - 5:16pm

MDF will host a strategic workshop this fall for professionals from the Food and Drug Administration, academic research institutions and pharmaceutical companies interested in DM therapy development. This regulatory meeting will be the first of its kind for DM.

08/14/2015 - 1:58pm

As potential therapies for myotonic dystrophy move out of the realm of hypothetical and into clinical testing, there is an urgent need to better understand what will be required from a regulatory standpoint to approve new therapies for this disease.

08/13/2015 - 12:38pm

The 21st Century Cures Act (H.R. 6) is a rare bipartisan initiative launched by the House Energy and Commerce Committee. While there are many factors that drove this effort, fundamentally it was a recognition that despite significant medical progress, there are 10,000 known diseases or conditions, but we only have cures and treatments for 500 of them.

08/10/2015 - 12:40pm

Mike Hamlin reflects on launching the MDF Support Group in Washington, DC.

07/20/2015 - 9:56am

The MDF Annual Conference is the best place for families looking for the most current information available on disease management, networking opportunities and support. New this year is a track focused on the latest in DM research, as well as workshops, roundtables and other programs for researchers from industry and academia.