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April 23, 2019

Defective insulin signaling activation may underlie skeletal muscle wasting in DM1 and DM2.

April 23, 2019

Preclinical proof of concept is published for a small molecule strategy targeting toxic DM1 repeat-expanded RNA.

April 23, 2019

A recent study implicates RNAi driven by CUGexp as an independent mechanism in altered gene expression and pathogenesis of DM1.

April 23, 2019

The Myotonic Dystrophy Foundation is currently planning a workshop to address CNS involvement in DM1, DM2 and CDM, to be held on September 12, 2019, in conjunction with the 2019 MDF Annual Conference, September 13-14, in Philadelphia, PA.

April 23, 2019

Nationwide Children’s Hospital and Ohio State University have operated a 5-day myology training course for the last seven years.  The course includes common lectures in the mornings and separate clinical and laboratory tracks in the afternoons.

April 23, 2019

Recent announcements from three biotechnology and pharmaceutical companies reflect the increasing interest in and tractability of myotonic dystrophy for therapy development. Short summaries and links to the press releases are provided here.

April 11, 2019

Dr. Vincent Dion awarded $250,000 grant to pursue gene editing technology development to find a cure for DM.

April 11, 2019

The Myotonic Dystrophy Clinical Research Network (DMCRN) sites are currently conducting a critically-important research study designed to help drug developers successfully design clinical trials and understand how to assess the efficacy of potential therapies.

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