A summary from the clinical endpoint workshop focusing on CNS clinical presentations and meaningful endpoints in clinical trials for myotonic dystrophy.
Presented by: Eric Wang, PhD, Associate Professor, Molecular Genetics & Microbiology, University of Florida, MDF Medical and Scientific Advisory Committee, MDF National Advocacy Committee
Thank you to our 2025 MDF Conference Sponsors for helping make this event possible:
- Lead Sponsor: Avidity Biosciences
- Diamond Sponsors: Dyne Therapeutics and Arthex Biotech
- Platinum Sponsors: PepGen and Vertex Pharmaceuticals
- Gold Sponsor: Sanofi
- Bronze Sponsor: Lupin Neurosciences