This session explores gene discoveries, gain of function RNA, and the personalized DM therapies of tomorrow, the power of unified registries, and interventional strategies targeting the cause of DM.
Presenters:
- Maurice S. Swanson, PhD, Professor and Associate Director, Department of Molecular Genetics and Microbiology Center for NeuroGenetics and the Genetics Institute, University of Florida
- Guillaume Bassez, MD, PhD, Institut de Myologie, MDF Medical and Scientific Advisory Committee
- Antoine Mangin, PhD, Cardiff University, UK Dementia Research Institute
Thank you to our 2025 MDF Conference Sponsors for helping make this event possible:
- Lead Sponsor: Avidity Biosciences
- Diamond Sponsors: Dyne Therapeutics and Arthex Biotech
- Platinum Sponsors: PepGen and Vertex Pharmaceuticals
- Gold Sponsor: Sanofi
- Bronze Sponsor: Lupin Neurosciences