2019 Myotonic Annual Conference Agenda

Friday, September 13

    • 7:30 - 8:30

      Professional's Breakfast
      A light breakfast and coffee.

    • 8:30 - 9:45
      DM Biomarkers: Goals, What's Working & How They'll Be Used for Drug Development & Approval moderated by Charles Thornton, MD, University of Rochester.
      • Frank Bennett, PhD, Ionis Pharmaceuticals
      • Donovan Lott, PhD, PT, University of Florida
      • Peg Nopoulos, MD, University of Iowa
      • Jeffrey Statland, MD, University of Kansas
      • Matthew Tanner, MS, University of Rochester
      • Thurman Wheeler, MD, Massachusetts General Hospital
    • 9:45 - 10:00

      Coffee Break

    • 10:00 - 12:00

      Current Therapeutic Approaches moderated by Douglas Kerr, MD, PhD, MBA, Generation Bio.

      • Andrew Berglund, PhD, RNA Institute
      • Vincent Dion, PhD, Cardiff University School of Medicine
      • Matthew Disney, PhD, Scripps Research Institute
      • Steve Finkbeiner, MD, PhD, Gladstone Institutes
      • Darren Monckton, PhD, University of Glasgow
      • Christopher Pearson, PhD, Hospital for Sick Children
      • Romesh Subramanian, PhD, Dyne Therapeutics
      • Eugene Yeo, PhD, UCSD/Locana Bio
    • 12:00 - 12:30

      Lunch (Provided)

    • 13:00 - 13:30

      DM2 State of the Science: Current Research, Next Steps with Allison Formal, MBA.

    • 13:30 - 15:00

      Study & Trial Learnings to Date – Observations on Design, Endpoints & Patient Enrichment Strategies moderated by Kathie Bishop, PhD, Otonomy.

      • Guillaume Bassez, MD, PhD, Institut de Myologie
      • Chad Heatwole, MD, University of Rochester
      • Joseph Horrigan, MD, AMO Pharma
      • Laurence Mignon, PhD, Ionis Pharmaceuticals
      • Christopher Turner, MD, PhD, University College London
    • 15:00 - 15:15


    • 15:15 - 15:45

      PRMRP: Specifics of This International Research Funding Program & Strategies for Application with Jonathan Ryder, PhD, US Department of Defense

    • 15:45 - 17:30

      DM Animal Models: What We Have, What We Need & Why moderated by Thomas Cooper, MD, Baylor College of Medicine.

      • Laurent Bogdanik, PhD, The Jackson Labs
      • Genèvieve Gourdon, PhD, Institut de Myologie
      • Sharon Hesterlee, PhD, AskBio
      • Laura Ranum, PhD, University of Florida
      • Ashish Rao, MS, Baylor College of Medicine
      • Maurice Swanson, PhD, University of Florida
      • Charles Thornton, MD, University of Rochester
      • Eric Wang, PhD, University of Florida
      • Thurman Wheeler, MD, Massachusetts General Hospital
    • 17:30 - 19:30

      Welcome Reception
      Join community members and DM professionals at the opening reception. Hors d'oeuvres will be served and a cash bar will be available. Be sure to visit the research poster session that will occur during the reception.

    • 17:30 - 19:30

      Research Poster Sessions (During Welcome Reception)
      MDF research Fellows, industry professionals and academic researchers present their current research and answer questions via 1:1 discussions at their posters. Grab a beverage and circulate!

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