December 2018 Research News
- Lessons Learned: Targeting RNA as a Therapeutic Strategy
- A Novel Genome Editing Strategy for DM1
- Drug Development Informed with TACT
- SAVE THE DATE: IDMC-12, June 2019
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
November 2018 Research News
- Challenges in Assessing the CNS in DM1
- Corticospinal Tract Involvement in DM1
- Mechanism of Myogenic Defects in CDM
- AMO Pharma Press Release Provides Its Analysis of Phase 2 Study Results
- SAVE THE DATE: IDMC-12, June 2019
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
October 2018 Research News
- Non-Invasive Biomarkers for DM1
- Review: What Have We Learned About RAN Translation?
- Scn5a and Cardiac Conduction in DM
- Myotonic Dystrophy Approved for Important 2019 Defense Funding Program!
- SAVE THE DATE: IDMC-12, June 2019
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- Recent DM Research Publications (Subscribe to DM Research News for details)
September 2018 Research News
- DM1 Care Recommendations Published
- Status: Clinical Outcome Measures for DM2
- Human iPSC-Derived Neurons for DM2
- Furamidine Mechanism of Action in DM1
- SAVE THE DATE: IDMC-12, June 2019
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August 2018 Research News
- MDF Releases RFA for DM1 Genome Editing Research
- NIAMS Releases New Funding Opportunities
- Modifiers of MBNL-Dependent Splicing in Health and Disease
- Fuchs’ Corneal Dystrophy in DM1 Patients Lacking the Fuchs’ Mutation
- DM1 Phenotype Modified by Repeat Interruptions
- Join Academic and Industry Colleagues at the 2018 MDF Annual Conference
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July 2018 Research News
- Therapeutic Gene Modulation: Targeting Muscleblind's Regulation by miRs
- OPTIMISTIC View of DM1
- NAS Releases Report on Patient Involvement in Research
- NIH Evaluates Wellstone Muscular Dystrophy Research Centers Program
- Richard T. Moxley, III, MD Tribute Program
- Join Academic and Industry Colleagues at the 2018 MDF Annual Conference
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
June 2018 Research News
- PRMRP - A New Funding Source for DM Research
- Senators Play Key Role in Getting DM Access to New Federal Research Funds
- Join Academic and Industry Colleagues at the 2018 MDF Annual Conference
- Mechanisms of Muscle Wasting in DM1
- Similar Molecular Mechanisms, but Divergent Phenotypes in DM1 and DM2 - Why?
- Important New Review Articles on DM
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
May 2018 Research News
- Join Academic and Industry Colleagues at the 2018 MDF Annual Conference
- Update: Research Funding Opportunity from the PRMRP
- New Release: NINDS Preclinical Translational Research Funding
- Quantifying Mutant mRNA in DM1 and DM2
- Microsatellite Expansions Selective Trigger Intron Retention
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
April 2018 Research News
- New Release: Research Funding Opportunity from the PRMRP
- Regulation of MBNL1 Localization and Function in the CNS
- Using iPSC-Derived Cardiomyocytes to Understand DM1
- NHGRI Genomic Medicine Research Initiative
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
March 2018 Research News
- Predictors of DM1 Patient Survival
- Determinants of Respiratory Function in DM1
- DM and the Canadian Neuromuscular Disease Registry
- Thanks Dr. John Porter, Welcome Dr. Lisa Ackermann!
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February 2018 Research News
- Comorbidity of Childhood DM1 and Autism?
- Imaging Neurocircuitry Changes in DM2 Mice
- The Future of Genetic Therapies
- Understanding the Functional Domains of MBNL
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)
January 2018 Research News
- MDF Receives $1M Grant to Launch Gene Editing Program for DM1
- New Biotech Company Announces Major Funding for DM Therapy Development
- MDF Funds Expansion of the DMCRN
- NIH Releases 2018 Funding Opportunities
- MDF and Wyck Award $300K in New Research Fellowships
- Toward 'Reponsive' Outcome Measures for DM1
- GSK3β As A Drug Development Target For DM1
- A Tool for Evaluating Drugs Targeting MBNL
- Funding Opportunities (Subscribe to DM Research News for details)
- Recent DM Research Publications (Subscribe to DM Research News for details)