Scientists from a consulting firm with considerable experience in evaluation of patient-reported outcome measures evaluated available PROMs for their potential in DM1 clinical trials.
New studies in mouse models show that constitutive or acquired loss of Dmpk has no effects on skeletal or cardiac muscle function.
A recent study corroborated increased susceptibility to cancer in DM1, for women in particular, and linked the elevated risk to depressed levels of a tumor suppressor microRNA (miRNA).
Acclaimed musician Eric Hutchinson is using his new album to support Care and a Cure. Read his inspiring family story.
AMO Pharma Limited (AMO Pharma) today announced initiation of a phase 2 clinical study in the U.K. for AMO-02 (tideglusib).