December 2023

• Give a Gift of Hope & Support MDF for the Holidays! 
• MDF is bringing the Conference to a City Near YOU in 2024! 
• Now Available - DM Research Landscape Assessment!
• Harmony Biosciences Announces Clinically Meaningful Improvements in Excessive Daytime Sleepiness & Fatigue in Adults with DM1 
• PepGen Announces Update on FREEDOM-DM1 Phase 1 Study!
• Leading DM Researcher & Professor, Cynthia Gagnon, PhD, Joins MDF Scientific Advisory Committee! 
• Welcome Andy Rohrwasser, PhD, MBA, as MDF’s Chief Scientific Officer! 
• ¡Ahora disponibles en Español! ¡Guía de ejercicios para personas con distrofia miotónica!
• Early Bird Registration Available Now for IDMC-14! 
• Increase Your Understanding of Myotonic Dystrophy (DM) with the Myotonic Dystrophy Family Registry! 
• Happy Holidays from Team MDF!

November 2023

• Recorded Sessions from the 2023 MDF Annual Conference Now Available Online!
• Start Celebrating the Holiday Season with #GivingTuesday
• Esteemed DM Researcher, Dr. Andy Berglund, Joins MDF Board of Directors & Chairs MDF's Scientific Advisory Committee.
  • Read more about what inspired Dr. Berglund to study DM!
• 2023 MDF Gala Raises $1.1 Million!
• Dyne Therapeutics Provides Update on Significant Progress for ACHIEVE Trial & Upcoming Clinical Milestones
• Avidity Biosciences Shares Clinical Trial Update with DM Community!
• PepGen Announces Update on FREEDOM-DM1 Phase 1 Study!
• Meet Emily Romney, MDF's New Special Projects Manager!
• Meet Genevieve Wiegleb, MDF's New Communications Associate!
• The Next Generation of DM Researchers Meet in New York
• Participating in the Myotonic Dystrophy Family Registry Helps DM Researchers! 
• Mark Your Calendars for IDMC-14! 

September 2023

• MDF Returns to Washington DC for Our Largest Conference Ever!
  • Learn more about the 2023 MDF Annual Conference!
• MDF Advocates Work to Secure Federal Myotonic Dystrophy Research Funding
  • Learn more about our incredible advocates and how you can get involved!
• DM2 Research Participation Opportunity: BraCE-DM2
• Watch the latest recording with AMO Pharma!
• Clearance of Defective Muscle Stem Cells by Senolytics Restores Myogenesis in DM1
• The World Glows Green in Celebration of International Myotonic Dystrophy Awareness Day!
  • Click here to see some of the amazing locations lit up by our Global Alliance. 
  • Learn how you can make a difference - click here to watch a recording on MDF's Advocacy Efforts!
  • What is International Myotonic Dystrophy Awareness Day? Click here to learn more about September 15!
• Download the New Foldable MDF Medical Alert Card!
• NEW: Clinical Recommendations for People of Pregnancy Potential!  
• Apply for 2024 MDF Research Fellowships & Early Career Grants
• Preview Our Fabulous Live Auction at the 2023 MDF Gala! 
• ¡Ahora disponibles en Español!
  • Chequea los documentos disponibles para el cuidado de pacientes con DM. Entre ellos están: la guía de manejo de la anestesia, atención médica de adultos con DM1, DM2 o niños, y así como recomendaciones para cardiólogos y pulmonólogos. ¡Clic aquí para recursos en español!
• Participating in the Myotonic Dystrophy Family Registry Helps DM Researchers! 
• Mark Your Calendars for IDMC-14! 

July 2023

• Download MDF's 2022 Report to the Community!
• Join us for our Meet the DM Drug Developers Webinar Series!
  • August 4th - Avidity Biosciences
  • Watch the latest recording with AMO Pharma!
• Clearance of Defective Muscle Stem Cells by Senolytics Restores Myogenesis in DM1
• Support Team Groovy Garibaldi's English Channel Relay Swim! 
• Download the New Foldable MDF Medical Alert Card!
• Join MDF for a Myotonic Dystrophy Day in Kansas City! 
• Apply for 2024 MDF Research Fellowships & Early Career Grants
• Celebrate International DM Awareness Day - Light Up Your Local Monuments in Green!
• You're Invited to the 2023 MDF Annual Conference!
  • Learn more about the announced speakers and sessions!
• Register for the 2023 MDF Gala!
• Update Your Myotonic Dystrophy Family Registry Profile Today!

June 2023

• Join us for our Meet the DM Drug Developers Webinar Series!
  • June 2nd - ARTHEx Biotech
  • June 9th - Dyne Therapeutics Preclinical Data
• Parent-of-Origin Effect on the Age at Symptom Onset in Myotonic Dystrophy Type 2
• Show You're Part of the Team with Myotonic Dystrophy In Motion Gear!
  • Last day to order is June 30th!
  • Find T-Shirts, water bottles, and more on the MDF Bonfire Store.
  • Join the movement - Myotonic Dystrophy In Motion!
• RNA Society Spotlight: Dr. Andrew Berglund
• Join MDF for a Myotonic Dystrophy Day in Kansas City!
• You're Invited to the 2023 MDF Annual Conference!
  • Early Bird registration extended to June 30th!
  • Discover the Conference Program
  • Calling all DM Professionals - Submit Your Research Poster Abstract!
• Be A Part of DM Research - Take the PSYQ-MD Survey!
• Meet Elias Trevino - Administrative Volunteer
• Mark Your Calendar for the 2023 MDF Gala!
• Get Connected with MDF Support Groups!
  • JOA Caregivers
  • DM2 Caregivers
  • CDM Caregivers
• Request for Applications Open - 2024 MDF Research Fellowships & Early Career Grants!
  • Read the Doctoral & Postdoctoral Fellowship RFA
  • Read the Early Career Research Grant RFA
• Meet Mindy Kim - Community Outreach Specialist
• Update Your Myotonic Dystrophy Family Registry Profile Today!
• My Featured Content:
  • Volunteer & Career Opportunities

May 2023

• Join us for our Meet the DM Drug Developers Webinar Series!

  • June 2nd - ARTHEx Biotech
  • June 9th - Dyne Therapeutics Preclinical Data
  • July 7th - AMO Pharma
  • Aug 4th - Avidity Biosciences

  Watch our most recent recordings:

  • PepGen
  • Avidity Biosciences Topline Data
• Download the Myotonic Dystrophy Anesthesia Guidelines - Ahora en Español!
  • Download the English one-page Quick Reference Guide./a>
  • Haga clic aquí para descargar las Pautas para la anestesia en Español.
• DMPK-promoter Silencing by CRISPRi a Promising Therapeutic Approach for DM1.
• Join MDF for a Myotonic Dystrophy Day in Kansas City!
• Show You're Part of the Team with Myotonic Dystrophy In Motion Gear!
  • Last day to order is June 16th!
  • Find T-Shirts, water bottles, and more on the MDF Bonfire Store.
  • Join the movement - Myotonic Dystrophy In Motion!
• Structure-forming CAG/CTG repeats interfere with gap repair to cause repeat expansions and chromosome breaks.
• You're Invited to the 2023 MDF Annual Conference!
  • Early Bird registration for the 2023 MDF Annual Conference ends June 19th!
  • Looking for Childcare at the 2023 MDF Annual Conference?
  • Calling all DM Professionals - Submit Your Research Poster Abstract!
• DM Research Grant Feature - Melissa Hale, PhD
• DM Research Fellow Feature - Jiss Louis, PhD
• Mark Your Calendar for the 2023 MDF Gala!
• Get Connected with MDF Support Groups!
  • JOA Caregivers
  • DM2 Caregivers
  • CDM Caregivers
• Thank You Jennifer Kang! 2022-2023 MDF Intern
  • Find a Doctor Map
• Request for Applications Open - 2024 MDF Research Fellowships & Early Career Grants!
  • Read the Doctoral & Postdoctoral Fellowship RFA
  • Read the Early Career Research Grant RFA
• Update Your Myotonic Dystrophy Family Registry Profile Today!
• My Featured Content:
  • Volunteer & Career Opportunities

April 2023

• Request for Applications Open - 2024 MDF Research Fellowships & Early Career Grants!
  • Read the Doctoral & Postdoctoral Fellowship RFA
  • Read the Early Career Research Grant RFA
• Join us for our Meet the DM Drug Developers Webinar Series!
  • April 7th - Dyne Therapeutics
  • May 5th - PepGen
  • June 2nd - ARTHEx Biotech
  • July 7th - AMO Pharma
  • Aug 4th - Avidity Biosciences
• Guide DM1 & DM2 Drug Development - Take the ENSA Survey!
  • ¿Prefiere español? ¡Pulse aquí si está interesado en participar!
• MGH Uses Targeted Drug to Restore Muscle Strength and Correct Myotonia in Mice with DM1
  • Read the Open Access article on Nature.com.
• Investigating the safety of baliforsen (ISIS 598769), an ASO targeting DMPK mRNA.
• You're Invited to the 2023 MDF Annual Conference!
  • Register Now for the 2023 MDF Annual Conference
  • New this year! Be the bridge between the DM Community and Research Professionals!
• Join Us Each Day Next Week During MDF Advocacy Week
• DM Research Grant Feature - Matteo Garibaldi, MD, PhD
• DM Research Grant Feature - Dylan Farnsworth, PhD
• Save the Date for IDMC-14
• Be a Part of the Myotonic Dystrophy Family Registry’s 10th Anniversary Celebration!
• Applications for Summer Internships at MDF Open Now!
• MDF Continues Search for Chief Science Officer!
• My Featured Content:
  • Download the Myotonic Dystrophy Anesthesia Guidelines
  • Volunteer & Career Opportunities

March 2023

• Global Alliance of 57+ Myotonic Dystrophy Focused Organizations Unite to Raise Awareness on Rare Disease Day 2023
• Join us for our Meet the DM Drug Developers Webinar Series!
  • April 7th - Dyne Therapeutics
  • May 5th - PepGen
  • June 2nd - ARTHEx Biotech
  • July 7th - AMO Pharma
  • Aug 4th - Avidity Biosciences
• Be A Part of DM Research - Take the PSYQ-MD Survey!
• Join Us for MDF's Advocacy Week
• DM Research Fellow Feature - Tatiana Koike, PhD
• DM Research Fellow Feature - Emma Shea
• #RAREis College Scholarship Fund by the Everylife Foundation
  • Did you know MDF Community Member Nick Gulch received a 2022 #RAREis Scholarship Award
• Access Our Video Catalog on the MDF Digital Academy!
  • Are you a DM Researcher looking for more funding? Watch Applying for PRMRP Funding!
  • Learn how to engage your representatives with support from MDF with our Advocacy Workshop.
• Does Your Doctor Understand Myotonic Dystrophy?
  • Fill your care team with myotonic dystrophy experts
  • Help improve our Find a Doctor Map
• Have You Joined the Myotonic Dystrophy Family Registry?
• MDF Continues Search for Chief Science Officer!
• Applications for Summer Internships at MDF Open Now!
• My Featured Content:
  • Download the Myotonic Dystrophy Anesthesia Guidelines
  • Volunteer & Career Opportunities

February 2023

• February is Rare Disease Month!
  • Applying for Myotonic Dystrophy Research Funding: Peer Reviewed Medical Research Program (PRMRP)
  • Learn how to engage your representatives with support from MDF at our Advocacy Workshop
  • Celebrate the Rare Disease Community and use your voice to make a difference on February 28th!
• Save the Date for the 2023 MDF Annual Conference!
  • Join us September 7th, 8th, & 9th in Washington, DC
  • Check our highlight video from the 2022 MDF Annual Conference
• Welcome Mindy Buchanan, Director of Programs
• Does Your Doctor Understand Myotonic Dystrophy?
  • Fill your care team with myotonic dystrophy experts
  • Help improve our Find a Doctor Map
• DM Research Fellow Feature - Mackenzie Davenport, PhD
• DM Research Fellow Feature - Julie Fortin, PhD
• Community Interview: Julie & Alex, MDF's Support Group Facilitators for Canada
• Community Interview: Araceli Mera & David Kugler, MDF’s Spanish-language Support Group Facilitators
• Have You Joined the Myotonic Dystrophy Family Registry?
• MDF Announces Search for Chief Science Officer
• My Featured Content: MDF is recruiting volunteer leaders and employees!

January 2023

• In Remembrance of Dad: 王望塵 - Reynold Wantseng Wang
• Congress Ensures DM Remains Eligible For PRMRP Research Funding For Sixth Year in A Row
  • DM Researchers Awarded Record $8.8 Million in New Awards In Fiscal Year 2022
  • Use Your Voice to Make a Difference! Join MDF for our Rare Disease Month Advocacy Workshop
• Welcome Sofia Olmos, PhD, Myotonic Dystrophy Family Registry Coordinator
  • Join the Myotonic Dystrophy Family Registry (MDFR)
• New Sites Recruiting for Harmony Biosciences DM1 Trial
  • Sites are now recruting in over 14 states in the US and Canada!
  • Find DM research participation opportunities on the MDF Study & Trial Resource Center
• Be a Part of the END-DM1 Study
• Community Interview: Glenda Winson, Guillermo Zubillaga & Jan Jaffe, New York City MDF Support Group Facilitators
• Community Interview: Jodie Howell & Samantha Welsh, Virginia State MDF Support Group Facilitators
• My Featured Content:
  • Volunteer & Career Opportunities with MDF
  • Join the Movement: International Myotonic Dystrophy Awareness Day